Table 5 Estimated numbers of RPE65-RD cases per center in the country (min–max).
From: Current management of inherited retinal degenerations in Portugal (IRD-PT survey)
Biallelic mutations | Patients eligible for treatment | Percentage of patients treated with neparvovec* | |
|---|---|---|---|
Min | 1 | 1 | 0% |
Max | 20 | 10 | 75% |
